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Veronica Ferrer

Explore the profile of Veronica Ferrer including associated specialties, affiliations and a list of published articles. Areas
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Articles 13
Citations 136
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Recent Articles
1.
Llanos-Ardaiz A, Lantero A, Neri L, Mauleon I, Ruiz de Galarreta M, Trigueros-Motos L, et al.
Int J Mol Sci . 2024 Dec; 25(23). PMID: 39684442
Adeno-associated viral (AAV) vector-mediated gene therapy has emerged as a promising alternative to liver transplantation for monogenic metabolic hepatic diseases. AAVs are non-integrative vectors that are maintained primarily as episomes...
2.
Murillo O, Collantes M, Gazquez C, Moreno D, Hernandez-Alcoceba R, Barberia M, et al.
Mol Ther Methods Clin Dev . 2022 Jul; 26:98-106. PMID: 35795774
Wilson's disease (WD) is an inherited disorder of copper metabolism associated with mutations in gene. We have shown that the administration of an adeno-associated vector (AAV) encoding a mini version...
3.
Ros-Ganan I, Hommel M, Trigueros-Motos L, Tamarit B, Rodriguez-Garcia E, Salas D, et al.
Clin Transl Immunology . 2022 Mar; 11(2):e1375. PMID: 35228870
Objective: Pre-existing neutralising antibodies (NAbs) to adeno-associated viruses (AAVs) remain an impediment for systemically administered AAV-mediated gene therapy treatment in many patients, and various strategies are under investigation to overcome...
4.
Weber N, Odriozola L, Martinez-Garcia J, Ferrer V, Douar A, Benichou B, et al.
Nat Commun . 2019 Dec; 10(1):5694. PMID: 31836711
Progressive familial intrahepatic cholestasis type 3 (PFIC3) is a rare monogenic disease caused by mutations in the ABCB4 gene, resulting in a reduction in biliary phosphatidylcholine. Reduced biliary phosphatidylcholine cannot...
5.
Murillo O, Moreno D, Gazquez C, Barberia M, Cenzano I, Navarro I, et al.
Hepatology . 2019 Feb; 70(1):108-126. PMID: 30706949
Gene therapy with an adeno-associated vector (AAV) serotype 8 encoding the human ATPase copper-transporting beta polypeptide (ATP7B) complementary DNA (cDNA; AAV8-ATP7B) is able to provide long-term copper metabolism correction in...
6.
Counsell J, Asgarian Z, Meng J, Ferrer V, Vink C, Howe S, et al.
Sci Rep . 2017 Aug; 7:46880. PMID: 28849794
This corrects the article DOI: 10.1038/srep44775.
7.
Counsell J, Asgarian Z, Meng J, Ferrer V, Vink C, Howe S, et al.
Sci Rep . 2017 Mar; 7:44775. PMID: 28303972
Duchenne Muscular Dystrophy (DMD) is caused by a lack of dystrophin expression in patient muscle fibres. Current DMD gene therapy strategies rely on the expression of internally deleted forms of...
8.
Counsell J, Asgarian Z, Meng J, Ferrer V, Vink C, Howe S, et al.
Sci Rep . 2017 Mar; 7(1):79. PMID: 28250438
Duchenne Muscular Dystrophy (DMD) is caused by a lack of dystrophin expression in patient muscle fibres. Current DMD gene therapy strategies rely on the expression of internally deleted forms of...
9.
Latorre G, Besa P, Parodi C, Ferrer V, Azocar L, Quirola M, et al.
Digestion . 2014 Aug; 90(1):18-26. PMID: 25096822
Background And Study Aims: Lactase non-persistence (LNP), or primary hypolactasia, is a genetic condition that mediates lactose malabsorption and can cause lactose intolerance. Here we report the prevalence of lactose...
10.
Carr A, Tamai T, Young L, Ferrer V, Dekens M, Whitmore D
Chronobiol Int . 2006 May; 23(1-2):91-100. PMID: 16687283
Zebrafish are typically used as a model system to study various aspects of developmental biology, largely as a consequence of their ex vivo development, high degree of transparency, and, of...