Sarmah D, Husson S
Membranes (Basel). 2024; 14(9).
PMID: 39330535
PMC: 11434191.
DOI: 10.3390/membranes14090194.
McColl-Carboni A, Dollive S, Laughlin S, Lushi R, MacArthur M, Zhou S
Gene Ther. 2024; 31(5-6):285-294.
PMID: 38374348
PMC: 11090809.
DOI: 10.1038/s41434-024-00444-2.
Pan Y, Rohde M, Zeitler J, Namburi S, Cao L, Hu J
Mol Ther Methods Clin Dev. 2023; 31:101126.
PMID: 37920239
PMC: 10618111.
DOI: 10.1016/j.omtm.2023.101126.
Ajenjo J, Seo J, Foiret J, Wu B, Raie M, Wang J
Theranostics. 2023; 13(15):5151-5169.
PMID: 37908737
PMC: 10614693.
DOI: 10.7150/thno.85549.
Tejero M, Duzenli O, Caine C, Kuoch H, Aslanidi G
Genes (Basel). 2023; 14(10).
PMID: 37895215
PMC: 10606878.
DOI: 10.3390/genes14101866.
Adeno-associated viral capsid stability on anion exchange chromatography column and its impact on empty and full capsid separation.
Khanal O, Kumar V, Jin M
Mol Ther Methods Clin Dev. 2023; 31:101112.
PMID: 37868210
PMC: 10585339.
DOI: 10.1016/j.omtm.2023.101112.
Prospective approaches to gene therapy computational modeling - spotlight on viral gene therapy.
Choules M, Bonate P, Heo N, Weddell J
J Pharmacokinet Pharmacodyn. 2023; 51(5):399-416.
PMID: 37848637
PMC: 11576656.
DOI: 10.1007/s10928-023-09889-1.
N-glycomic profiling of capsid proteins from Adeno-Associated Virus serotypes.
Xie Y, Butler M
Glycobiology. 2023; 34(1).
PMID: 37774344
PMC: 10950483.
DOI: 10.1093/glycob/cwad074.
Size Exclusion Chromatography-Mass Photometry: A New Method for Adeno-Associated Virus Product Characterization.
Wu D, Zhao X, Jimenez D, Piszczek G
Cells. 2023; 12(18).
PMID: 37759487
PMC: 10528216.
DOI: 10.3390/cells12182264.
Correlating physicochemical and biological properties to define critical quality attributes of a rAAV vaccine candidate.
Kumar P, Wang M, Kumru O, Hickey J, Sanmiguel J, Zabaleta N
Mol Ther Methods Clin Dev. 2023; 30:103-121.
PMID: 37746246
PMC: 10512015.
DOI: 10.1016/j.omtm.2023.06.004.
Design space determination to optimize DNA complexation and full capsid formation in transient rAAV manufacturing.
Fu Q, Suk Lee Y, Green E, Wang Y, Park S, Polanco A
Biotechnol Bioeng. 2023; 120(11):3148-3162.
PMID: 37475681
PMC: 11585969.
DOI: 10.1002/bit.28508.
Large-scale purification of functional AAV particles packaging the full genome using short-term ultracentrifugation with a zonal rotor.
Wada M, Uchida N, Posadas-Herrera G, Hayashita-Kinoh H, Tsunekawa Y, Hirai Y
Gene Ther. 2023; 30(7-8):641-648.
PMID: 36977769
PMC: 10457186.
DOI: 10.1038/s41434-023-00398-x.
Immunogenicity assessment of AAV-based gene therapies: An IQ consortium industry white paper.
Yang T, Braun M, Lembke W, McBlane F, Kamerud J, DeWall S
Mol Ther Methods Clin Dev. 2022; 26:471-494.
PMID: 36092368
PMC: 9418752.
DOI: 10.1016/j.omtm.2022.07.018.
Current Advances in Adeno-Associated Virus-Mediated Gene Therapy to Prevent Acquired Hearing Loss.
Wu F, Sambamurti K, Sha S
J Assoc Res Otolaryngol. 2022; 23(5):569-578.
PMID: 36002664
PMC: 9613825.
DOI: 10.1007/s10162-022-00866-y.
FSHD Therapeutic Strategies: What Will It Take to Get to Clinic?.
Himeda C, Jones P
J Pers Med. 2022; 12(6).
PMID: 35743650
PMC: 9225474.
DOI: 10.3390/jpm12060865.
Assessment of the percentage of full recombinant adeno-associated virus particles in a gene therapy drug using CryoTEM.
Colomb-Delsuc M, Raim R, Fiedler C, Reuberger S, Lengler J, Nordstrom R
PLoS One. 2022; 17(6):e0269139.
PMID: 35657790
PMC: 9165851.
DOI: 10.1371/journal.pone.0269139.
Characterization of Recombinant Chimpanzee Adenovirus C68 Low and High-Density Particles: Impact on Determination of Viral Particle Titer.
Mullins E, Powers T, Zobel J, Clawson K, Barnes L, Draper B
Front Bioeng Biotechnol. 2021; 9:753480.
PMID: 34805110
PMC: 8599148.
DOI: 10.3389/fbioe.2021.753480.
Comparison of analytical techniques to quantitate the capsid content of adeno-associated viral vectors.
Werle A, Powers T, Zobel J, Wappelhorst C, Jarrold M, Lyktey N
Mol Ther Methods Clin Dev. 2021; 23:254-262.
PMID: 34703846
PMC: 8505359.
DOI: 10.1016/j.omtm.2021.08.009.
Analytical band centrifugation for the separation and quantification of empty and full AAV particles.
Khasa H, Kilby G, Chen X, Wang C
Mol Ther Methods Clin Dev. 2021; 21:585-591.
PMID: 34095342
PMC: 8142049.
DOI: 10.1016/j.omtm.2021.04.008.
Comparison of Different Liquid Chromatography-Based Purification Strategies for Adeno-Associated Virus Vectors.
Rieser R, Koch J, Faccioli G, Richter K, Menzen T, Biel M
Pharmaceutics. 2021; 13(5).
PMID: 34070226
PMC: 8158740.
DOI: 10.3390/pharmaceutics13050748.
