» Articles » PMID: 38882014

Dominant Negative Effect As a Novel Mechanism of SPAST Gene Mutation in a Large Family with Hereditary Spastic Paraplegia

Overview
Journal Genes Dis
Date 2024 Jun 17
PMID 38882014
Authors
Affiliations
Soon will be listed here.
References
1.
Julien C, Lissouba A, Madabattula S, Fardghassemi Y, Rosenfelt C, Androschuk A . Conserved pharmacological rescue of hereditary spastic paraplegia-related phenotypes across model organisms. Hum Mol Genet. 2016; 25(6):1088-99. PMC: 4764191. DOI: 10.1093/hmg/ddv632. View

2.
Li L, Yang X . Tubulin acetylation: responsible enzymes, biological functions and human diseases. Cell Mol Life Sci. 2015; 72(22):4237-55. PMC: 11113413. DOI: 10.1007/s00018-015-2000-5. View

3.
Rehbach K, Kesavan J, Hauser S, Ritzenhofen S, Jungverdorben J, Schule R . Multiparametric rapid screening of neuronal process pathology for drug target identification in HSP patient-specific neurons. Sci Rep. 2019; 9(1):9615. PMC: 6610147. DOI: 10.1038/s41598-019-45246-4. View

4.
Solowska J, DRozario M, Jean D, Davidson M, Marenda D, Baas P . Pathogenic mutation of spastin has gain-of-function effects on microtubule dynamics. J Neurosci. 2014; 34(5):1856-67. PMC: 3905148. DOI: 10.1523/JNEUROSCI.3309-13.2014. View

5.
Depienne C, Stevanin G, Brice A, Durr A . Hereditary spastic paraplegias: an update. Curr Opin Neurol. 2007; 20(6):674-80. DOI: 10.1097/WCO.0b013e3282f190ba. View