6.
Brousseau D, Scott J, Badaki-Makun O, Darbari D, Chumpitazi C, Airewele G
. A multicenter randomized controlled trial of intravenous magnesium for sickle cell pain crisis in children. Blood. 2015; 126(14):1651-7.
PMC: 4591790.
DOI: 10.1182/blood-2015-05-647107.
View
7.
Krishnamurti L, Neuberg D, Sullivan K, Kamani N, Abraham A, Campigotto F
. Bone marrow transplantation for adolescents and young adults with sickle cell disease: Results of a prospective multicenter pilot study. Am J Hematol. 2019; 94(4):446-454.
PMC: 6542639.
DOI: 10.1002/ajh.25401.
View
8.
Badawy S, Thompson A, Holl J, Penedo F, Liem R
. Healthcare utilization and hydroxyurea adherence in youth with sickle cell disease. Pediatr Hematol Oncol. 2019; 35(5-6):297-308.
DOI: 10.1080/08880018.2018.1505988.
View
9.
Cunningham N, Kashikar-Zuck S, Mara C, Goldschneider K, Revicki D, Dampier C
. Development and validation of the self-reported PROMIS pediatric pain behavior item bank and short form scale. Pain. 2017; 158(7):1323-1331.
PMC: 5996986.
DOI: 10.1097/j.pain.0000000000000914.
View
10.
Singh S, Bakshi N, Mahajan P, Morris C
. What is the future of patient-reported outcomes in sickle-cell disease?. Expert Rev Hematol. 2020; 13(11):1165-1173.
PMC: 7722233.
DOI: 10.1080/17474086.2020.1830370.
View
11.
Singh A, Dasgupta M, Simpson P, Brousseau D, Panepinto J
. Can PROMIS domains of pain and physical functioning detect changes in health over time for children with sickle cell disease?. Pediatr Blood Cancer. 2020; 67(5):e28203.
DOI: 10.1002/pbc.28203.
View
12.
Dampier C, Jaeger B, Gross H, Barry V, Edwards L, Lui Y
. Responsiveness of PROMIS® Pediatric Measures to Hospitalizations for Sickle Pain and Subsequent Recovery. Pediatr Blood Cancer. 2016; 63(6):1038-45.
PMC: 5055833.
DOI: 10.1002/pbc.25931.
View
13.
Bakshi N, Ross D, Krishnamurti L
. Presence of pain on three or more days of the week is associated with worse patient reported outcomes in adults with sickle cell disease. J Pain Res. 2018; 11:313-318.
PMC: 5810514.
DOI: 10.2147/JPR.S150065.
View
14.
Steinberg M, Barton F, Castro O, Pegelow C, Ballas S, Kutlar A
. Effect of hydroxyurea on mortality and morbidity in adult sickle cell anemia: risks and benefits up to 9 years of treatment. JAMA. 2003; 289(13):1645-51.
DOI: 10.1001/jama.289.13.1645.
View
15.
Rees C, Brousseau D, Cohen D, Villella A, Dampier C, Brown K
. Sickle Cell Disease Treatment with Arginine Therapy (STArT): study protocol for a phase 3 randomized controlled trial. Trials. 2023; 24(1):538.
PMC: 10433602.
DOI: 10.1186/s13063-023-07538-z.
View
16.
Panepinto J, Scott J, Badaki-Makun O, Darbari D, Chumpitazi C, Airewele G
. Determining the longitudinal validity and meaningful differences in HRQL of the PedsQL™ Sickle Cell Disease Module. Health Qual Life Outcomes. 2017; 15(1):124.
PMC: 5468970.
DOI: 10.1186/s12955-017-0700-2.
View
17.
Singh A, Dasgupta M, Simpson P, Panepinto J
. Use of the new pediatric PROMIS measures of pain and physical experiences for children with sickle cell disease. Pediatr Blood Cancer. 2019; 66(5):e27633.
DOI: 10.1002/pbc.27633.
View
18.
Farrell A, Panepinto J, Carroll C, Darbari D, Desai A, King A
. End points for sickle cell disease clinical trials: patient-reported outcomes, pain, and the brain. Blood Adv. 2019; 3(23):3982-4001.
PMC: 6963237.
DOI: 10.1182/bloodadvances.2019000882.
View
19.
Reyes L, Figueroa J, Leake D, Khemani K, Kumari P, Bakshi N
. Safety of intravenous arginine therapy in children with sickle cell disease hospitalized for vaso-occlusive pain: A randomized placebo-controlled trial in progress. Am J Hematol. 2021; 97(1):E21-E24.
PMC: 8722015.
DOI: 10.1002/ajh.26396.
View
20.
Platt O, Thorington B, Brambilla D, Milner P, Rosse W, Vichinsky E
. Pain in sickle cell disease. Rates and risk factors. N Engl J Med. 1991; 325(1):11-6.
DOI: 10.1056/NEJM199107043250103.
View