Safety, Efficacy, and Authorization of Eliglustat As a First-line Therapy in Gaucher Disease Type 1

Overview

Journal Blood Cells Mol Dis

Specialty Hematology

Date 2018 Apr 23

PMID 29680197

Citations 12

Authors

Pramod K Mistry

Manisha Balwani

Hagit N Baris

Hadhami Ben Turkia

T Andrew Burrow

Joel Charrow

Gerald F Cox

Sumita Danda

Marta Dragosky

Guillermo Drelichman

Amal El-Beshlawy

Cristina Fraga

Selena Freisens

Sebastiaan Gaemers

Evgueniy Hadjiev

Priya S Kishnani

Elena Lukina

Pierre Maison-Blanche

Ana Maria Martins

Gregory Pastores

Milan Petakov

M Judith Peterschmitt

Hanna Rosenbaum

Barry Rosenbloom

Lisa H Underhill

Timothy M Cox

Affiliations

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