Securing Reimbursement for Patient Centered Haemophilia Care: Major Collaborative Efforts Are Needed

Overview

Journal Haematologica

Specialty Hematology

Date 2016 Mar 2

PMID 26928247

Citations 2

Authors

Karin C Berger

Brian M Feldman

Joan Wasserman

Wolfgang Schramm

Victor Blanchette

Kathelijn Fischer

Affiliations

Soon will be listed here.

Citing Articles

Kreuth V initiative: European consensus proposals for treatment of hemophilia using standard products, extended half-life coagulation factor concentrates and non-replacement therapies.

Peyvandi F, Berger K, Seitz R, Hilger A, Hecquet M, Wierer M Haematologica. 2020; 105(8):2038-2043.

PMID: 32467138 PMC: 7395279. DOI: 10.3324/haematol.2019.242735.

Strategies for eliciting and synthesizing evidence for guidelines in rare diseases.

Pai M, Yeung C, Akl E, Darzi A, Hillis C, Legault K BMC Med Res Methodol. 2019; 19(1):67.

PMID: 30922227 PMC: 6437842. DOI: 10.1186/s12874-019-0713-0.

References

Atkins D, Best D, Briss P, Eccles M, Falck-Ytter Y, Flottorp S . Grading quality of evidence and strength of recommendations. BMJ. 2004; 328(7454):1490. PMC: 428525. DOI: 10.1136/bmj.328.7454.1490. View

Mahdi A, Obaji S, Collins P . Role of enhanced half-life factor VIII and IX in the treatment of haemophilia. Br J Haematol. 2015; 169(6):768-76. DOI: 10.1111/bjh.13360. View

OMahony B, Black C . Expanding hemophilia care in developing countries. Semin Thromb Hemost. 2005; 31(5):561-8. DOI: 10.1055/s-2005-922228. View

Donadel-Claeyssens S . Current co-ordinated activities of the PEDNET (European Paediatric Network for Haemophilia Management). Haemophilia. 2006; 12(2):124-7. DOI: 10.1111/j.1365-2516.2006.01202.x. View

Fischer K, Grobbee D, van den Berg H . RCTs and observational studies to determine the effect of prophylaxis in severe haemophilia. Haemophilia. 2007; 13(4):345-50. DOI: 10.1111/j.1365-2516.2007.01521.x. View

Drummond M, Schwartz J, Jonsson B, Luce B, Neumann P, Siebert U . Key principles for the improved conduct of health technology assessments for resource allocation decisions. Int J Technol Assess Health Care. 2008; 24(3):244-58. DOI: 10.1017/S0266462308080343. View

Chitlur M, Warrier I, Rajpurkar M, Lusher J . Inhibitors in factor IX deficiency a report of the ISTH-SSC international FIX inhibitor registry (1997-2006). Haemophilia. 2009; 15(5):1027-31. DOI: 10.1111/j.1365-2516.2009.02039.x. View

Dreyer N, Schneeweiss S, McNeil B, Berger M, Walker A, Ollendorf D . GRACE principles: recognizing high-quality observational studies of comparative effectiveness. Am J Manag Care. 2010; 16(6):467-71. View

Tunis S, Benner J, McClellan M . Comparative effectiveness research: Policy context, methods development and research infrastructure. Stat Med. 2010; 29(19):1963-76. DOI: 10.1002/sim.3818. View

10.

Makris M, Calizzani G, Fischer K, Gilman E, Hay C, Lassila R . EUHASS: The European Haemophilia Safety Surveillance system. Thromb Res. 2011; 127 Suppl 2:S22-5. DOI: 10.1016/S0049-3848(10)70150-X. View

11.

Balshem H, Helfand M, Schunemann H, Oxman A, Kunz R, Brozek J . GRADE guidelines: 3. Rating the quality of evidence. J Clin Epidemiol. 2011; 64(4):401-6. DOI: 10.1016/j.jclinepi.2010.07.015. View

12.

Walley T . Translating comparative effectiveness research into clinical practice: the UK experience. Drugs. 2012; 72(2):163-70. DOI: 10.2165/11630860-000000000-00000. View

13.

Sox H, Goodman S . The methods of comparative effectiveness research. Annu Rev Public Health. 2012; 33:425-45. DOI: 10.1146/annurev-publhealth-031811-124610. View

14.

Greenfield S, Platt R . Can observational studies approximate RCTs?. Value Health. 2012; 15(2):215-6. DOI: 10.1016/j.jval.2012.01.003. View

15.

Berger M, Dreyer N, Anderson F, Towse A, Sedrakyan A, Normand S . Prospective observational studies to assess comparative effectiveness: the ISPOR good research practices task force report. Value Health. 2012; 15(2):217-30. DOI: 10.1016/j.jval.2011.12.010. View

16.

Hershman D, Wright J . Comparative effectiveness research in oncology methodology: observational data. J Clin Oncol. 2012; 30(34):4215-22. DOI: 10.1200/JCO.2012.41.6701. View

17.

Evatt B . Demographics of hemophilia in developing countries. Semin Thromb Hemost. 2005; 31(5):489-94. DOI: 10.1055/s-2005-922218. View